Dystonia Research
What is dystonia?
Dystonia is a movement disorder, often characterized by twisting movements and abnormal postures resulting from involuntary muscle spasms. It can affect multiple areas (generalized dystonia) or one area (focal dystonia).
Current Trials
Dose-escalation Study: A Phase 1 dose escalation study to evaluate the safety, tolerability, and pharmacokinetics of co-administration of two medications in healthy adult volunteers and adults with isolated dystonia.
Observational Study: This non-interventional observational study is designed to assess motor symptoms and disease burden in individuals with isolated dystonia by characterizing and quantifying changes in clinical features over a period of up to four months. In addition, the study will enhance the understanding of clinical outcomes scale performance.